Anaemia Aplastic Anaemia Congenital Dyserythropoietic Anaemia Fanconi Anaemia Paroxysmal Nocturnal Haemoglobinuria (PNH)
Inherited Disorders Amegakaryocytosis / Congenital Thrombocytopenia Beta Thalassemia Major Cartilage-Hair Hypoplasia Diamond-Blackfan Anaemia Glanzmann Thrombasthenia Gunther's Disease (Erythropoietic Porphyria) Hermansky-Pudlak Syndrome Hurler's Syndrome (MPS-IH) Hunter's Syndrome (MPS-II) Maroteaux-Lamy Syndrome (MPS-VI) Morquio Syndrome (MPS-IV) Mucolipidosis II (I-cell Disease) Mucopolysaccharidoses (MPS) Omenn Syndrome Pearson's Syndrome Pure Red Cell Aplasia Sanfilippo Syndrome (MPS-III) Scheie Syndrome (MPS-IS) SCID with Adenosine Deaminase Deficiency (ADA-SCID) SCID which is X-linked SCID with absence of T and B Cells SCID with absence of T Cells, Normal B Cells Shwachman-Diamond Syndrome Sickle Cell Disease Systemic Mastocytosis Sly Syndrome, Beta-Glucuronidase Deficiency (MPS-VII)
Leukaemia Acute Lymphoblastic Leukaemia (ALL) Acute Myelogenous Leukaemia (AML) Acute Biphenotypic Leukaemia Acute Undifferentiated Leukaemia Chronic Myelogenous Leukaemia (CML) Chronic Myelomonocytic Leukemia (CMML) Chronic Lymphocytic Leukaemia (CLL) Juvenile Chronic Myelogenous Leukaemia (JCML) Juvenile Myelomonocytic Leukaemia (JMML) Refractory Anaemia (RA) Refractory Anaemia with Ringed Sideroblasts (RARS) Refractory Anaemia with Excess Blasts (RAEB) Refractory Anaemia with Excess Blasts in Transformation (RAEB-T)
Leukodystrophy Disorders Adrenoleukodystrophy (ALD) / Adrenomyeloneuropathy (AMN) Krabbe Disease (Globoid Cell Leukodystrophy) Metachromatic Leukodystrophy Pelizaeus-Merzbacher Disease
Myeloproliferative Disorders Acute Myelofibrosis Agnogenic Myeloid Metaplasia (Myelofibrosis) Essential Thrombocythemia
Phagocyte Disorders Chediak-Higashi Syndrome Chronic Granulomatous Disease Neutrophil Actin Deficiency Reticular Dysgenesis
Other Ataxia-Telangiectasia Bare Lymphocyte Syndrome Common Variable Immunodeficiency DiGeorge Syndrome Hemophagocytic Lymphohistiocytosis Lesch-Nyhan Syndrome Leukocyte Adhesion Deficiency Lymphoproliferative Disorders (LPD) Lymphoproliferative Disorder, X-linked Osteopetrosis Wiskott-Aldrich Syndrome
Autoimmune Disorders Amyotrophic Lateral Sclerosis (ALS) Crohn's Disease Diabetes Type 1 Graft-versus-Host-Disease (GVHD) Kidney Plus Stem Cell Transplant Lupus Multiple Sclerosis Rheumatoid Arthritis Scleroderma
Cardiovascular Cardiomyopathy Critical Limb Ischemia (CLI) Compartment Syndrome (Battlefield Trauma) Hypoplastic Left Heart Syndrome (HLHS) Grow Vascular Graft Ischemic Heart Disease Ischemic stroke Myocardial Infarction Support for Misc. Open Heart Surgery
Gene Therapies Adrenoleukodystrophy AIDS & HIV Alveolar Cleft Palate Repair Bronchopulmonary Dysplasia (BPD) Chronic Granulomatous Disease (X-linked) Epidermolysis Bullosa Fanconi Anaemia Knee Cartilage Repair Lysosomal Storage Disease Metachromatic Leukodystrophy Severe Combined Immunodeficiency Sickle Cell Thalassemia Wiskott-Aldrich Syndrome
Neurological Disorder Autism Cerebral Palsy Hearing Loss (acquired sensorineural) Hypoxic Ischemic Encephalopathy (HIE) Spinal Cord Injury